Webinars

After the Trial: What next? Getting a drug into a clinic

Tuesday 30th June 2026 @ 7pm

Via Zoom

Presenter: Professor Richard Keen, Royal National Orthopaedic Hospital

Following recent positive clinical trial results, Regeneron and Incyte/Mirum are advancing their respective applications for market approval in the USA.

Professor Richard Keen will discuss what these developments mean for patients and families across the UK. He will outline the pathways pharmaceutical companies must navigate to achieve UK market access, beginning with regulatory approval from the Medicines and Healthcare products Regulatory Agency (MHRA), moving through the role of the National Institute for Health and Care Excellence (NICE), and specifically highlighting the Highly Specialised Technologies (HST) evaluation process. Finally, he will explain how these medicines ultimately reach patients through NHS England funding and commissioning frameworks.

The webinar will conclude with a Q&A session, offering an opportunity for attendees to ask questions.

Please note: Programme subject to change

What’s Taking So Long? The Realities of Developing FOP Treatments

Thursday 10th July 2025 @ 8pm 

Via Zoom link

Presenter: Dr Andrew Rankin, Trustee

Our first webinar aims to demystify the complex journey of developing drugs for Fibrodysplasia Ossificans Progressiva (FOP) and provide current information on treatment opportunities.

The webinar will cover:

The Journey of a Medicine: From initial ideas and understanding FOP’s biology to early lab research and crucial pre-clinical testing for safety and efficacy before human trials.

Navigating Clinical Trials: A detailed explanation of the different phases of clinical trials (Phase 1, 2, 3, and 4), what each phase entails, why they are necessary, and how they lead to regulatory approval.

Considerations for Patient Participation: What patients can expect when participating in a clinical trial

Current FOP Clinical Trials & Treatment Opportunities: An overview of the current landscape of FOP research, highlighting different therapeutic approaches and specific ongoing trials.

Attendees are invited to send in questions before the event. The webinar will also conclude with a Q&A session

Please note: Programme subject to change